Home News Drug to treat genetic disorder that causes rapid aging in kids approved...

Drug to treat genetic disorder that causes rapid aging in kids approved by FDA



A new drug to treat a rare genetic disorder that causes rapid aging in children has been approved after clinical studies showed promising results in extending their lives.

Zokinvy, the first drug of its kind to treat the genetic mutation known as progeria that also stunts growth, was approved by the US Food and Drug Administration this week. In clinical tests, the drug was found to increase patients’ lives by more than two years.

There are an estimated 400 people around the world and 20 in the US who suffer from the condition which causes hair loss and aged-looking skin. Children afflicted with the disease suffer strokes and hardening of arteries and typically die at 14.

The disorder is not inherited but due to a chance gene mutation that causes a damaging buildup in cells of a protein called progeria,

Research on the treatment was mainly funded by the Progeria Research Foundation in Peabody, Mass., with help from drug developer Eiger BioPharmaceuticals.

LEAVE A REPLY

Please enter your comment!
Please enter your name here

Most Popular

Madonna gives fans a rare look at all six of her children in family holiday photos

She has a lovely blended family including two biological children from prior relationships and four adopted children from Malawi, Africa.But it's a rare...

No charges to be filed in death of Cornell freshman ‘hazed’ at frat party

No criminal charges will be filed in the death of a Cornell University freshman whose body was found in an Ithaca gorge last...

The Walking Dead showrunner drops huge clue that Heath will return: 'On my list'

With plenty more Walking Dead to come, Corey Hawkins could eventually reprise his role in the eleventh and final instalment of the flagship...

Money Heist season 5 theories: The Professor makes huge sacrifice in tragic series finale

User SamLFC89 posted: “I can just imagine the last scenes being Palermo saying ‘it was an honour’ to the Professor.“Then everyone sings Bella...

Recent Comments